Orion Therapeutics
RNA technology thus has the potential to revolutionize medicine with life-saving and even curative treatments for previously unmet clinical needs, including cancers, autoimmune disorders, and neurodegenerative diseases. The primary bottleneck in the translation of the 1300+ early-stage RNA programs in existence has been the biological delivery system, not the RNA drug payload itself, due to toxicity, immunogenicity, and the inability to target specific cells, tissues, and organs, leading to off-target effects.
